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Rare diseases deeply affect not only the children who experience them, but also their healthy brothers and sisters, as their parents can attest.    Two entries in November’s “Disorder: The Rare Disease Film Festival” will focus on what siblings go through, according to the San Francisco festival’s co-founder,…

Developing gene therapies for rare diseases is one thing. Creating gene-edited “designer babies” is quite another. German legal expert Timo Minssen outlined the potentially explosive ethical landmines surrounding such issues during a recent talk at the New York Genome Center. Minssen directs the Center for Advanced Studies in…

Researchers recently reported the rare case of a 69-year-old Japanese man with paroxysmal atrial fribrillation (PAF) — occasional periods of an irregular, very fast heart rate — who developed hyperkalemia (high potassium levels in the blood) possibly due to cold agglutinin disease (CAD) after undergoing cryoballoon ablation…

A recent case report alerts clinicians to the fact that cold agglutinin disease (CAD) can arise as a complication of Pneumococcal vaccination. This is the first documented case of an adult who developed CAD associated with a specific self-reactive antibody (anti-Pr) following pneumococcal vaccination. The study, “Anti-Pr…