News Phase 3 Data Support Safety, Efficacy of Sutimlimab in Treating CAD

News Rare Disease Film Festival Highlights Patient and Researcher Unity

News Risk of Blood Clots Higher in CAD Patients Than General Population, Study Concludes

News Combo That Includes Hyperbaric Oxygen Treats Nose Ischemia Linked to CAD, Report Says

News Arzerra a Potential Alternative to Rituxan for Patients with AIHA and Lupus, Case Report Suggests

News Earlier Meningitis Vaccine Booster May be Necessary for CAD Patients on Anti-complement Therapy, Study Suggests

News Review Looks at AIHA Risk, Treatment Options in Patients After Stem Cell Transplant

News NORD 2019 Rare Disease Summit Set for Oct. 21-22 in Washington, DC

News Study Finds Risk Factors for AIHA Following Stem Cell Transplant

News Be on Lookout for CAD, Other Conditions That May Affect Cancer Surgery, Physicians Advised

News ‘Disorder’ Film Festival Offers Look at Siblings Touched by Rare Diseases

News At NY Genome Center, Legal Expert Presents Ethical Dilemmas in Gene Editing

News Study Reports Rare Case of CAD Arising After Cryoablation Therapy

News Nebraska’s Neena Nizar Seeks Cure for Jansen’s, One of World’s Rarest Diseases

News Report Describes Rare Case of CAD Linked to Pneumococcal Vaccination in Adult

News New Study Identifies Risk Factors for AIHA in Patients with Genetic Blood Disease

News Rare Disease Groups Seek Public Support to Renew Newborn Screening Act in Senate

News Oklahoma Ranks Lowest on Programs Key to Rare Diseases on NORD’s 2019 State Report Card

News EBV Infection Can Cause Cold Agglutinin Disease, Even Without Symptoms of Infection, Case Study Suggests

News Rare Cancer May Trigger Cold Agglutinin Hemolytic Anemia, Case Report Suggests

News European Initiative Targets Diagnosis, Treatment of Rare Diseases

News CAD-induced Hemolytic Anemia May Be Manifestation of SLE, Study Reports

News Macedonian Gaucher Activist Publicizes Plight of Rare Disease Patients

News World’s First Alport Stamp Is Macedonian Mom’s Latest Win for Rare Disease Patients

News Targeting Complement System May Help Halt Autoimmune Hemolytic Anemia, Study Suggests

News NORD Honors Industry, Patient Advocates at Rare Impact Awards Gala

News APL-2 Increases Hemoglobin Levels, Reduces Hemolysis in CAD and wAIHA Patients, Trial Results Shows

News Eurordis Unveils Integrated-care Initiative for Rare Disease Patients

News ‘Rare Barometer’ Program Helps Eurordis Shape EU Rare Disease Policy

News Awareness Needed for Successful Dental Management of CAD Patients, Report Highlights

News Agency Unveils RaDaR to Help Patient Groups Develop Rare Disease Registries

News Rare Diseases Constitute a ‘Public Health Issue,’ NCATS Director Warns

News Case Study of Cold AIHA and Rare B-cell Leukemia Suggests Possible ‘Innovative’ Therapies

News Rare Case of Multiple Myeloma in Patient with Cold Agglutinin Disease Described in Report

News Review Addresses Rituxan and Bendamustine as First-line Treatment for CAD

News Closely Monitoring CAD Patients Helps Prevent Dangerous Complications in Heart Surgery, Study Says

News Bortezomib Shows Promise for Treating Certain CAD Patients, Phase 2 Trial Finds

News CAD Patients Have Twice the Mortality Risk Within First 5 Years of Diagnosis, Study Reports

News Keytruda Can Trigger Blood Disorders Including AIHA, Rare Case Suggests

News Brexit Could Have Real Effects for UK Rare Disease Patients, Experts Warn

News Moral Dilemmas Complicate Treatment of Rare Diseases, Says Israeli Bioethicist

News NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research

News Apellis, SFJ Partnering on APL-2 Development for Treatment of CAD, wAIHA

News WODC 2019 Organizers Expect 1,200 to Attend Rare Disease Conference in April

News Vienna to Host RARE2019 Meeting on Rare Diseases

News 1st Case of CAD Linked to Anti-Cancer Treatment Tecentriq Reported

News Patients, Family and Friends to Take Part in Variety of Rare Disease Day Events Worldwide

News Study Urges Careful Analysis of MAIHA Patients to Optimize Treatment

News Apellis’ APL-2 Receives FDA’s Orphan Drug Designation for AIHA

News CAD Caused Red Blood Cells’ Abnormal Distribution, Report Suggests

News FDA Revising ‘Draft Guidance’ on Developing Treatments for Rare Diseases

News Coexistence of Cryoglobulinemic Vasculitis and CAD Described for 1st Time in Case Report

News CAD, wAIHA Patients May Benefit from Different Rituxan Doses, Study Suggests

News Cold Hemolytic Anemia a Rare Possibility in Mononucleosis Patients, Case Report Shows

News Targeting Complement Pathway May Offer New Therapies for CAD

News Report Details Rare Case of Acute Kidney Injury in CAD Patient Who Drank Heavily

News Soliris Therapy Eases Hemolysis and Blood Transfusion Needs in CAD Patients, Phase 2 Trial Shows

News Soliris May Be Effective Off-Label Treatment for CAD Attacks, Case Report Suggests

News Sutimlimab Increases Hemoglobin Levels in Patients with Cold Agglutinin Disease, First-in-human Trial Shows

News #NORDSummit – Major Issues on Table for Rare Disease Patients in US as Midterm Elections Approach

News Advocacy Groups, Doctors Question Rising Prices of Rare Disease Treatments

News #NORDSummit – More Than 700 Expected to Attend Oct. 15-16 Rare Disease Summit in Washington

News US ‘Right to Try’ Law Meets with Mix of Praise and Criticism, Including Among Those with Rare Diseases

News #ERDC2018 – When Treating Rare Disease Patients, Don’t Overlook Quality of Life, Panel Urges

News ‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35

News #ECRD2018 – EU Must Do More for Rare Disease Patients, Eurordis Leaders Say

News #ECRD2018 – Patient Access and Collaboration Focus of Eurordis Meeting May 10-12

News NIH Agency Pioneers Collaborative Research into Rare Diseases

News Genome Sequencing and Its Clinical Potential Focus of NYC Rare Disease Day Event

News ‘A Disease May Be Rare, Hope Should Never Be,’ Says Boy with SMARD at Connecticut Rare Disease Day Event

News Rare Disease Groups Welcome FDA’s Embrace of ‘Real World’ Data in Clinical Trials

News US Lawmakers Urge Bipartisan Support for Rare Disease Research, Patients’ Needs

News Retrophin, Horizon Donate $3M Each to Rare Disease Institute at Children’s National

News BioNews to Cover 3 Rare Disease Day Events, Including NIH Conference

News Patient Advocacy Groups Worldwide Plan Events to Mark Rare Disease Day, Feb. 28

News Rare Disease Groups, Patients Differ on ‘Right to Try’ Bill Before US Congress

News NORD Fundraiser Sets 7,000-Mile ‘Bike, Run or Walk’ Goal for 7,000 Rare Diseases